FDA Approves First RNA-Targeted Therapy for HAE
- SSCTR Exco
- Aug 25, 2025
- 1 min read
Published on: LinkedIn (Spencer Knight)
The U.S. FDA has approved DAWNZERA (donidalorsen) from Ionis Pharmaceuticals, the first RNA-targeted prophylactic therapy for hereditary angioedema (HAE) in patients 12 years and older. Clinical trials showed up to 90% reduction in moderate-to-severe attacks and long-term durability, offering new hope for the 7,000 people in the U.S. living with this rare, life-threatening condition.
👉 Read the full article: First-in-Class Breakthrough in HAE
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